| Adenovirus-Mediated Somatic Genome Editing of Pten by CRISPR/Cas9 in Mouse Liver in Spite of Cas9-Specific Immune Responses D Wang, H Mou, S Li, Y Li, S Hough, K Tran, J Li, H Yin, DG Anderson, ... Human gene therapy 26 (7), 432-442, 2015 | 383 | 2015 |
| MicroRNA 122, regulated by GRLH2, protects livers of mice and patients from ethanol-induced liver disease A Satishchandran, A Ambade, S Rao, YC Hsueh, A Iracheta-Vellve, ... Gastroenterology 154 (1), 238-252. e7, 2018 | 139 | 2018 |
| Empty virions in AAV8 vector preparations reduce transduction efficiency and may cause total viral particle dose-limiting side effects K Gao, M Li, L Zhong, Q Su, J Li, S Li, R He, Y Zhang, G Hendricks, ... Molecular Therapy-Methods & Clinical Development 1, 2014 | 132 | 2014 |
| Short DNA hairpins compromise recombinant adeno-associated virus genome homogeneity J Xie, Q Mao, PWL Tai, R He, J Ai, Q Su, Y Zhu, H Ma, J Li, S Gong, ... Molecular Therapy 25 (6), 1363-1374, 2017 | 111 | 2017 |
| A rationally engineered capsid variant of AAV9 for systemic CNS-directed and peripheral tissue-detargeted gene delivery in neonates D Wang, S Li, DJ Gessler, J Xie, L Zhong, J Li, K Tran, K Van Vliet, L Ren, ... Molecular Therapy Methods & Clinical Development 9, 234-246, 2018 | 55 | 2018 |
| Adeno-associated virus neutralizing antibodies in large animals and their impact on brain intraparenchymal gene transfer D Wang, L Zhong, M Li, J Li, K Tran, L Ren, R He, J Xie, RP Moser, ... Molecular Therapy-Methods & Clinical Development 11, 65-72, 2018 | 49 | 2018 |
| Adeno-associated virus serotype rh. 10 displays strong muscle tropism following intraperitoneal delivery J Ai, J Li, DJ Gessler, Q Su, Q Wei, H Li, G Gao Scientific Reports 7 (1), 40336, 2017 | 47 | 2017 |
| Cas9-mediated allelic exchange repairs compound heterozygous recessive mutations in mice D Wang, J Li, CQ Song, K Tran, H Mou, PH Wu, PWL Tai, CA Mendonca, ... Nature biotechnology 36 (9), 839-842, 2018 | 42 | 2018 |
| rAAV gene therapy in a Canavan’s disease mouse model reveals immune impairments and an extended pathology beyond the central nervous system. GG Seemin Seher Ahmed, Stefan A. Schattgen, Ashley E. Frakes , Elif M ... Molecular Therapy, 2016 | 40 | 2016 |
| Gene Transfer in the Liver Using Recombinant Adeno‐Associated Virus SS Ahmed, J Li, J Godwin, G Gao, L Zhong Current protocols in microbiology 29 (1), 14D. 6.1-14D. 6.32, 2013 | 40 | 2013 |
| Circumventing cellular immunity by miR142-mediated regulation sufficiently supports rAAV-delivered OVA expression without activating humoral immunity Y Xiao, M Muhuri, S Li, W Qin, G Xu, L Luo, J Li, AJ Letizia, SK Wang, ... JCI insight 4 (13), 2019 | 33 | 2019 |
| Intravenous Infusion of AAV for Widespread Gene Delivery to the Nervous System DJGPWLTJLG Gao Adeno-Associated Virus Vectors, 2019 | 33* | 2019 |
| Differential proteomics and functional research following gene therapy in a mouse model of Leber congenital amaurosis Q Zheng, Y Ren, R Tzekov, Y Zhang, B Chen, J Hou, C Zhao, J Zhu, ... Public Library of Science 7 (8), e44855, 2012 | 19 | 2012 |
| Slow infusion of recombinant adeno-associated viruses into the mouse cerebrospinal fluid space D Wang, J Li, K Tran, DR Burt, L Zhong, G Gao Human Gene Therapy Methods 29 (2), 75-85, 2018 | 9 | 2018 |
| High-Throughput Quantification of In Vivo Adeno-Associated Virus Transduction with Barcoded Non-Coding RNAs M Xu, J Li, J Xie, R He, Q Su, G Gao, PWL Tai Human Gene Therapy 30 (8), 946-956, 2019 | 6 | 2019 |
| Characterization of adenoviral transduction profile in prostate cancer cells and normal prostate tissue J Ai, PWL Tai, Y Lu, J Li, H Ma, Q Su, Q Wei, H Li, G Gao The Prostate 77 (12), 1265-1270, 2017 | 2 | 2017 |
| In vivo suppressor tRNA mediated readthrough therapy for nonsense mutations C Mendonca, L Ren, J Li, Y Zhang, J Min, J Wang, Q Su, G Gao, D Wang Mol. Ther 28, 120, 2020 | 1 | 2020 |
| dCas13-Mediated Therapeutic RNA Base Editing for In Vivo Gene Therapy J Wang, L Ren, J Li, G Gao, D Wang MOLECULAR THERAPY 28 (4), 38-39, 2020 | 1 | 2020 |
| Developing a rAAV-Based Gene Replacement Therapy for GM3 Synthase Deficiency H Yang, K Brigatti, J Li, M Dookwah, M Tiemeyer, D Wang, KA Strauss, ... MOLECULAR THERAPY 28 (4), 91-91, 2020 | | 2020 |
| Developing AAV-Mediated Clinically Translatable Gene Therapy for Maple Syrup Urine Disease (MSUD) Caused by BCKDHA Mutations in a Bovine Model J Wang, E Puffenberger, J Beever, H GrayEdwards, J Li, RM Wynn, ... MOLECULAR THERAPY 28 (4), 411-412, 2020 | | 2020 |
